Luxturna is a gene therapy.
The generic name of Luxturna is “voretigene neparvovec-rzyl”
Luxturna is a treatment for people who have Leber congenital amaurosis (LCA) or retinitis pigmentosa (RP) caused by mutations in both copies of the RPE65 gene. Luxturna provides a working copy of the RPE65 gene to restore the visual cycle. This allows photoreceptor cells in the retina to sense light and send a message to the brain. Evidence from clinical trials shows that this treatment can safely improve vision, particularly night vision and the ability to function independently.
Luxturna is a one-time treatment that can improve sight (especially night vision) and the ability to function independently.